Nearly 30 people attended CTSI's quarterly Science Cafe on Sept. 22 to hear about new therapies and alternative treatments used in clinical trials to treat rare genetic neurological disorders.
Chester Whitley, M.D., Ph.D. provided a detailed overview of clinical research that has led to improved health for those affected by rare genetic and metabolic disorders such as Hunter syndrome, Tay-Sachs disease, Sanfilippo syndrome, Gaucher disease and Hurler syndrome.